Infantile Malignant Osteopetrosis clinical trials at University of California Health
1 research study open to eligible people
A Trial to Evaluate Safety and Efficacy of RP-L401-0120 in Subjects With Infantile Malignant Osteopetrosis
open to eligible people ages 1 month and up
The primary objective of this Phase 1 study is to evaluate the therapeutic safety and feasibility of the investigational product (IP), RP-L401.