Alpha Thalassemia Major clinical trials at University of California Health
2 in progress, 1 open to eligible people
open to all eligible people
This is an international prospective registry of patients with Alpha thalassemia to understand the natural history of the disease and the outcomes of fetal therapies, with the overall goal of improving the prenatal management of patients with Alpha thalassemia.
Sorry, in progress, not accepting new patients
The investigators aims to evaluate the safety of in utero hematopoietic stem cell transplantation in fetuses with alpha-thalassemia major performed at the time of in utero transfusion of red blood cells.
Our lead scientists for Alpha Thalassemia Major research studies include Tippi C MacKenzie, MD.