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Charcot-Marie-Tooth Disease clinical trials at UC Health
1 research study open to new patients

  • Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease

    open to eligible people ages 18 years and up

    This is a multicenter, phase 2 study to evaluate the safety, tolerability, pharmacodynamics (PD), efficacy, and pharmacokinetics (PK) of ACE-083 in patients with CMT1 and CMTX, to be conducted in two parts. Part 1 is non-randomized, open-label, dose-escalation and Part 2 is randomized, double-blind, and placebo-controlled.

    at UC Irvine

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