Gene Therapy clinical trials at University of California Health
1 research study open to eligible people
Showing trials for
Lentiviral Gene Transfer for SCID-X1 with Low Dose Targeted Busulfan Conditioning
open to eligible males ages 0-5
This is a phase I/II open label multi-center study in which patients will receive low dose targeted busulfan followed by infusion of autologous CD34+ selected bone marrow or mobilized peripheral blood cells transduced with the G2SCID vector.…
at UCLA
Our lead scientists for Gene Therapy research studies include Satiro De Oliveira, MD.
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