Late-onset Pompe Disease clinical trials at UC Health
1 in progress, 0 open to new patients
Sorry, in progress, not accepting new patients
The purpose of the study is to evaluate changes in key clinical outcome measures (eg, motor, respiratory, fatigue) in adult subjects with late-onset Pompe disease (LOPD) subjects receiving standard-of-care enzyme replacement therapy (ERT). Additionally, information gained may be used in the design and conduct of future studies in LOPD subjects.
at UC Irvine