Progressive Familial Intrahepatic Cholestasis clinical trials at University of California Health

2 in progress, 1 open to eligible people

A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
open to all eligible people
This study is designed to assess whether the investigational drug maralixibat, is safe and well tolerated in children <12 months of age with Alagille Syndrome [ALGS] or Progressive Familial Intrahepatic Cholestasis [PFIC].
at UCSF
Long Term Safety & Efficacy Study Evaluating The Effect of A4250 in Children With PFIC
Sorry, in progress, not accepting new patients
Open Label Extension Study to evaluate long term safety and persistence of effect of A4250 in children with PFIC.
at UCSF

Last updated: October 10, 2022

A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).