Progressive Familial Intrahepatic Cholestasis clinical trials at University of California Health

2 in progress, 0 open to eligible people

Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
Sorry, in progress, not accepting new patients
This study is designed to assess whether the investigational drug maralixibat, is safe and well tolerated in children <12 months of age with Alagille Syndrome [ALGS] or Progressive Familial Intrahepatic Cholestasis [PFIC].
at UCSF
Long Term Safety & Efficacy Study Evaluating The Effect of A4250 in Children With PFIC
Sorry, in progress, not accepting new patients
Open Label Extension Study to evaluate long term safety and persistence of effect of A4250 in children with PFIC.
at UCSF

Last updated: September 5, 2023

Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).