Progressive Familial Intrahepatic Cholestasis clinical trials at University of California Health
3 in progress, 2 open to eligible people
A Study to Evaluate the Safety and Tolerability of Maralixibat in Infant Participants With Cholestatic Liver Diseases Including Progressive Familial Intrahepatic Cholestasis (PFIC) and Alagille Syndrome (ALGS).
open to all eligible people
This study is designed to assess whether the investigational drug maralixibat, is safe and well tolerated in children <12 months of age with Alagille Syndrome [ALGS] or Progressive Familial Intrahepatic Cholestasis [PFIC].
at UCSF
Long Term Safety & Efficacy Study Evaluating The Effect of A4250 in Children With PFIC
open to eligible people ages 0 months to 100 years
Open Label Extension Study to evaluate long term safety and persistence of effect of A4250 in children with PFIC.
at UCSF
A Study to Evaluate the Efficacy and Safety of Maralixibat in Subjects With Progressive Familial Intrahepatic Cholestasis (MARCH-PFIC)
Sorry, in progress, not accepting new patients
The purpose of this study is to determine if the investigational treatment (maralixibat) is safe and effective in pediatric participants with Progressive Familial Intrahepatic Cholestasis (PFIC).
at UCSF
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