Rett Syndrome clinical trials at University of California Health
2 in progress, 0 open to eligible people
Sorry, accepting new patients by invitation only
To investigate the safety and tolerability of continued long-term treatment with oral trofinetide in girls and women with Rett syndrome
at UC Davis UCSD
Sorry, not currently recruiting here
The Rett Syndrome Registry is a longitudinal observational study of individuals with MECP2 mutations and a diagnosis of Rett syndrome. Designed together with the IRSF Rett Syndrome Center of Excellence Network medical directors, this study collects data on the signs and symptoms of Rett syndrome as reported by the Rett syndrome experts and by the caregivers of individuals with Rett syndrome. This study will be used to develop consensus based guidelines for the care of your loved ones with Rett syndrome and to facilitate the development of better clinical trials and other aspects of the drug development path for Rett syndrome.