Stargardt Disease clinical trials at University of California Health
4 in progress, 2 open to eligible people
ALK-001 on Stargardt Disease
open to eligible people ages 8-70
The purpose of this study is to determine the long term safety and tolerability of ALK-001 (C20-D3-retinyl acetate), and to explore the effects of ALK-001 on the progression of Stargardt disease in patients between the ages of 8 and 70 years old. Funding Source - FDA OOPD
at UCLA
Observational Study in Subjects to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene
open to eligible people ages 12-65
This is an Observational Study to Follow the Progression of Stargardt Disease Type 1 (STGD1) Caused by Bi-Allelic Autosomal Recessive Mutations in the ABCA4 Gene This is a multicenter study which will enroll approximately 75 subjects
at UCSD
ACDN-01 in ABCA4-related Retinopathy (STELLAR)
Sorry, not currently recruiting here
This study is an open-label, single ascending dose clinical trial in participants who have ABCA4-related retinopathies. This is the first-in-human clinical trial in which ACDN-01 will be evaluated for safety, tolerability, and preliminary efficacy following a single subretinal injection of ACDN-01.
at UCSF
Zimura Compared to Sham in Patients With Autosomal Recessive Stargardt Disease (STGD1)
Sorry, in progress, not accepting new patients
The purpose of this study is to evaluate the safety and efficacy of avacincaptad pegol intravitreal injection compared to Sham in participants with autosomal recessive Stargardt disease 1 (STGD1).
at UCLA
Our lead scientists for Stargardt Disease research studies include Jacque Duncan Michael Gorin, MD, PhD.
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