Summary
The purpose of this study is to evaluate the efficacy, safety, and pharmacokinetics of mavacamten in adolescent patients with symptomatic obstructive hypertrophic cardiomyopathy (HCM).
Official Title
A Randomized, Double-blind, Placebo-controlled Clinical Study to Evaluate Mavacamten in Adolescents (Age 12 Years to < 18 Years) With Symptomatic Obstructive Hypertrophic Cardiomyopathy
Keywords
Cardiomyopathy, Hypertrophic, HCM, mavacamten, Obstructive Hypertrophic Cardiomyopathy, SCOUT, SCOUT-HCM, Pediatric HCM, Pediatric hypertrophic cardiomyopathy, Symptomatic HCM, oHCM, Cardiomyopathies, Hypertrophic Cardiomyopathy, Hypertrophy