Acute Porphyria clinical trials at UC Health

• Longitudinal Study of the Porphyrias

  open to all eligible people

  The objective of this protocol is to conduct a longitudinal multidisciplinary investigation of the human porphyrias including the natural history, morbidity, pregnancy outcomes, and mortality in people with these disorders.

  at UCLA UCSF

• ENVISION: A Study to Evaluate the Efficacy and Safety of Givosiran (ALN-AS1) in Patients With Acute Hepatic Porphyrias (AHP)

  Sorry, in progress, not accepting new patients

  The purpose of this study is to evaluate the effect of subcutaneous givosiran (ALN-AS1), compared to placebo, on the rate of porphyria attacks in patients with Acute Hepatic Porphyrias (AHP).

  at UCSF

Last updated: March 9, 2021