Summary

Eligibility
for people ages 18-65 (full criteria)
Location
at UCSF
Dates
study started
study ends around
Principal Investigator
by Irene Chang (ucsf)

Description

Summary

Official Title

A Phase 1/Phase 2, Open-label, Dose-escalation, and Dose Expansion Study to Evaluate the Safety, Tolerability, and Efficacy of SAR444836, an Adeno-associated Viral Vector-mediated Gene Transfer of Human Phenylalanine Hydroxylase, in Adult Participants With Phenylketonuria

Keywords

Phenylketonuria, Phenylketonurias, SAR444836

Eligibility

Locations

  • University of California San Francisco - Parnassus Heights- Site Number : 8400007 accepting new patients
    San Francisco California 94143 United States
  • Children's Hospital Colorado - Aurora- Site Number : 8400015 accepting new patients
    Aurora Colorado 80045 United States

Lead Scientist at University of California Health

  • Irene Chang (ucsf)
    Assistant Professor, Pediatrics, School of Medicine. Authored (or co-authored) 29 research publications

Details

Status
accepting new patients
Start Date
Completion Date
(estimated)
Sponsor
Sanofi
ID
NCT05972629
Phase
Phase 1/2 Phenylketonuria Research Study
Study Type
Interventional
Participants
Expecting 32 study participants
Last Updated